Success stories

Partnerships to success

Ghana FDA training

-A five-day training of the clinical assessors of Ghana FDA

- Topics covered included basis of bioequivalence, assessment of the modified-release dosage forms, bioanalysis and bioanalytical method validation, narrow therapeutic index drugs, highly variable drugs.

-Comparison of EMA and US FDA practices  

- Training included case studies and assessment of the dossiers

Justification of Tmax bioinequivalence

-Product-specific bioequivalence guideline in place for the molecule in question

- Tmax bioinequivalence raised as a major objection during the procedure

- Justification was based on clinical irrelevance and lack of PK/PD correlation

-Justification was accepted and the product was registered


Audit of a non-EU dossier of a complex formulation

- The dossier audit was ordered by an EU client for the purpose of in-licensing

- Reference product was not from EU, comparative PK study was performed in non-EU population

-Solution for a bridging strategy from non-EU to EU reference was recommended

- Extrapolation of the PK study results to Caucasian population was done to exclude the influence of genetic differences on the PK of the active substance

- The product was successfully registered

CMDh referral for modified-release dosage form

-In vitro dose dumping tested, release in alcohol different to the reference product. Major objection raised.

- Justification was based on the clinical significance of the dose dumping test findings.

- Clinical effects of the concomitant administration of a drug with alcohol were summarized in the response

- Additional in vitro data generated

-Referral successfully resolved, product obtained marketing authorisation

Medical writing for gastroresistant formulation

-Legal basis is well-established use, no PK or clinical data generated. Evidence on the PK, efficacy and safety of the product are based on the published literature

-The critical part of the Clinical Overview is bridging of the to-be-marketed product to the published evidence

- Comprehensive search of EU market for similar products performed

- Qualitative composition of marketed products was compared to the to-be-registered product

-Clinical consequences of bioinequivalence assessed

-No major objection raised on the bridging strategy